- Maria Gabelli,
- Antonio Marzollo,
- Lucia Dora Notarangelo,
- Giuseppe Basso,
- Maria Caterina Putti
Pediatr Blood Cancer 2017 Jun 23. Epub 2017 Jun 23.
Department of Women's and Children's Health, Pediatric Onco-Hematology Unit, University of Padova, Padova, Italy.
Wiskott-Aldrich syndrome (WAS) is an inherited X-linked disorder characterized by microthrombocytopenia, immunodeficiency, and eczema. Hematopoietic stem cell transplantation (HSCT) is the treatment of choice. Eltrombopag, a thrombopoietin receptor agonist, may be useful to prevent bleeding while awaiting HSCT. Read More