Pubfacts - Scientific Publication Data
  • Categories
  • |
  • Journals
  • |
  • Authors
  • Login
  • Categories
  • Journals

Search Our Scientific Publications & Authors

Publications
  • Publications
  • Authors
find publications by category +
Translate page:

Gonadal dysgenesis without adrenal insufficiency in a 46, XY patient heterozygous for the nonsense C16X mutation: a case of SF1 haploinsufficiency.

Authors:
Delphine Mallet Patricia Bretones Laurence Michel-Calemard Frederique Dijoud Michel David Yves Morel

J Clin Endocrinol Metab 2004 Oct;89(10):4829-32

Laboratoire de Biochimie Endocrinienne et Moléculaire, Hôpital Debrousse, and EA3739, Université Claude Bernard, Lyon, France.

Targeted disruption of the orphan nuclear receptor SF1 results in the absence of adrenals and gonads, establishing that this transcription factor is implicated in gonadal determination and adrenal development. Four human SF1 gene mutations have been described to date: three (G35E, R92Q, R255L) were responsible for adrenal insufficiency associated with a gonadal dysgenesis in two 46, XY individuals, one (8 bp deletion in exon 6) resulted in gonadal dysgenesis without adrenal insufficiency. We identified a new heterozygous SF1 gene mutation, C16X, in a 46, XY patient showing gonadal dysgenesis with normal adrenal function: low basal levels of AMH and testosterone (T), weak T response to hCG, hypoplastic testes with abundant seminiferous tubules but rare germ cells. This mutation causes premature termination of translation and should abolish all SF1 activity. Therefore haploinsufficiency could explain the deleterious effect of this mutation in our patient suggesting that testis development is more SF1 dose-dependent than adrenal development. Although the same mechanism explains the deleterious effects of SF1 missense mutations, recent studies have demonstrated an additional dominant negative effect. These data suggest that heterozygous mutation impaired adrenal development only if the two mechanisms, gene dosage and dominant negative effects occur.

Download full-text PDF

Source
http://dx.doi.org/10.1210/jc.2004-0670DOI Listing
October 2004

Publication Analysis

Top Keywords

gonadal dysgenesis
16
adrenal insufficiency
12
adrenal development
12
dominant negative
8
sf1 gene
8
dysgenesis adrenal
8
sf1
7
adrenal
7
gonadal
5
mutation
5
patient showing
4
showing gonadal
4
sf1 missense
4
basal levels
4
c16x patient
4
dysgenesis normal
4
normal adrenal
4
effects sf1
4
function low
4
adrenal function
4

Similar Publications

Scapular Winging Secondary to Serratus Anterior Dysfunction: Analysis of Clinical Presentations and Etiology in a Consecutive Series of 96 Patients.

Authors:
Chye Yew Ng Feiran Wu

J Shoulder Elbow Surg 2021 Mar 3. Epub 2021 Mar 3.

Dept of Orthopaedics, University Hospitals Birmingham, Mindelsohn Way, Birmingham, B15 2TH, UK.

Background: This study aimed to establish the relative incidence of etiologies causing serratus anterior (SA) dysfunction in patients with proven abnormality on needle electromyography.

Methods: This was a retrospective review of patients with scapular winging secondary to SA dysfunction. Each patient underwent a detailed clinical, radiological and neurophysiological assessment to arrive at the precise etiological diagnosis. Read More

View Article and Full-Text PDF
March 2021
Similar Publications

Prophylactic gonadectomy in 46 XY females; why, where and when?

Authors:
Nurul Iftida Basri Chong Hong Soon Anizah Ali Nur Azurah Abdul Ghani Ani Amelia Zainuddin

Horm Mol Biol Clin Investig 2021 Mar 8. Epub 2021 Mar 8.

Paediatric Adolescent Gynecology Unit, Department of Obstetrics and Gynecology, Universiti Kebangsaan Malaysia Medical Centre, Cheras, Malaysia.

Objectives: We compared cases of phenotypic female patients who presented with male karyotype and underwent prophylactic gonadectomy.

Case Presentation: Five patients with female phenotypes presented in early adulthood with primary amenorrhoea with varying degrees of puberty. One was tall with breast development. Read More

View Article and Full-Text PDF
March 2021
Similar Publications

Nephrotic syndrome secondary to alpha-1 antitrypsin deficiency.

Authors:
Gabriela F Santos Paul Ellis Daniela Farrugia Alice M Turner

BMJ Case Rep 2021 Mar 5;14(3). Epub 2021 Mar 5.

Respiratory Medicine, University Hospitals Birmingham NHS Foundation Trust, Birmingham, UK

We report a 64-year-old caucasian woman diagnosed with membranous nephropathy secondary to alpha-1 antitrypsin deficiency (AATD). AATD is a rare autosomal codominant genetic disorder. Its clinical manifestations are mostly observed in the lungs, with early-onset emphysema. Read More

View Article and Full-Text PDF
March 2021
Similar Publications

Ovotesticular disorder of sex development in Korean children: a single-center analysis over a 30-year period.

Authors:
Hye In Kim Inha Lee Sang Hwa Kim Yong Seoung Lee Sang Won Han Bo Hyon Yun

J Pediatr Adolesc Gynecol 2021 Mar 2. Epub 2021 Mar 2.

Department of Obstetrics and Gynecology, Severance Hospital, Yonsei University College of Medicine, 50 Yonsei-ro, Seodaemun-gu, Seoul 03722, Republic of Korea; Institute of Women's Life Science, Yonsei University College of Medicine, Seoul, Korea. Electronic address:

Study Objective: To present clinical features that characterize ovotesticular disorder of sex development (OT-DSD) in the Korean population. Among the patient cohort who were initially suspected of OT-DSD, the actual OT-DSD patients and those of other DSD were compared.

Design: Retrospective medical chart review of patients who were initially suspected of OT-DSD from 1984 to 2018 based on clinical examination. Read More

View Article and Full-Text PDF
March 2021
Similar Publications

"Anterior interosseous nerve syndrome (Kiloh Nevin Syndrome) revealing Gantzer muscle and simultaneous myasthenia gravis".

Authors:
J Musa M Rahman I Kola A Guy L Pena A Lekoubou F Hyseni L Compres K Saliaj R Blanco

Radiol Case Rep 2021 Apr 16;16(4):983-988. Epub 2021 Feb 16.

Centro Médico Vista del Jardin, Santo Domingo, Dominican Republic.

There hasn't been a previous case report of the anterior interosseous nerve injury secondary to the presence of the muscle of Gantzer in a patient with myasthenia gravis in literature before. The anterior interosseous nerve compressive syndrome, also known as Kiloh-Nevin syndrome, is a rare disorder comprising less than 1% of all upper limb neuropathies. Establishing the etiology of anterior interosseous nerve compressive syndrome is challenging because of the lack of specific clinical findings or testing. Read More

View Article and Full-Text PDF
April 2021
Similar Publications
© 2021 PubFacts.
  • About PubFacts
  • Privacy Policy
  • Sitemap