29 Publications
Cell Stem Cell 2021 Jan 25. Epub 2021 Jan 25.
Division of Hematology/Oncology, Boston Children's Hospital, Department of Pediatric Oncology, Dana-Farber Cancer Institute, Harvard Stem Cell Institute, Broad Institute, Department of Pediatrics, Harvard Medical School, Boston, MA 02115, USA. Electronic address:
N Engl J Med 2021 01 5;384(3):205-215. Epub 2020 Dec 5.
From the Dana-Farber/Boston Children's Cancer and Blood Disorders Center, Harvard Medical School (E.B.E., L.E.L., A.B., C.B., M.F.C., B.M., K.B., S.-Y.P., W.B.L., C.D., M.M.H., D.A.W.), the Harvard Stem Cell Institute, Harvard Medical School (A.B., C.B.), the Gene Therapy Program, Dana-Farber/Boston Children's Cancer and Blood Disorders Center (A.B., M.F.C., B.M., E.M., A.F., S.-Y.P., C.D., D.A.W.), the Division of Hematology, Brigham and Women's Hospital, Harvard Medical School (M. Achebe), the Connell and O'Reilly Families Cell Manipulation Core Facility, Dana-Farber Cancer Institute (H.D., R.K., K.S., H.N., S.N., J.R.), the TransLab, Boston Children's Hospital (D.A., M. Armant), and the Department of Laboratory Medicine, Boston Children's Hospital, Harvard Medical School (J.P.M.) - all in Boston; and Bluebird Bio, Cambridge, MA (O.N.).
Mol Ther Methods Clin Dev 2020 Jun 17;17:589-600. Epub 2020 Mar 17.
Division of Hematology/Oncology, Boston Children's Hospital, Boston, MA, USA.
Nat Med 2020 02 27;26(2):200-206. Epub 2020 Jan 27.
Great Ormond Street Institute of Child Health and Great Ormond Street Hospital NHS Foundation Trust, London, UK.
N Engl J Med 2019 10 9;381(17):1644-1652. Epub 2019 Oct 9.
From the Divisions of Genetics and Genomics (J.K., C.H., E.A.L., A.S., J.V., R.L.D., J.C., P.B.A., A.H.B., S.E.W., O.B., T.W.Y.), Newborn Medicine (P.B.A., P.E.G.), and Neuroradiology (P.E.G.), the Departments of Neurology (C.M.E.A., D.K.U., A. Poduri), Anesthesiology, Critical Care and Pain Medicine (L.C., C.B.B.), Physical and Occupational Therapy (A. Pasternak, E.R.B., K.A.P.), and Pharmacy (S.C., A. Patterson), the Institutional Centers for Clinical and Translational Research (A.K., B.B., L.W.), and the Manton Center for Orphan Disease Research (C.A.G., P.B.A., A.H.B.), Boston Children's Hospital (A.K., A.T., M.A., L.M.P., K.D., B.B., L.W., B.D.G., B.L.R., A.B.), the Department of Biomedical Informatics (J.K., P.J.P.), Harvard Medical School (J.K., C.M.E.A., E.A.L., L.C., B.D.G., B.L.R., P.B.A., A.H.B., P.E.G., D.K.U., S.E.W., P.J.P., A. Patterson, A.B., O.B., C.B.B., T.W.Y.), and the Gene Therapy Program (A.B.), Boston Children's and Dana-Farber Cancer and Blood Disorders Center (A.K., B.B., L.W.), Boston, Charles River Laboratories, Wilmington (L.E.B.), and Broad Institute of MIT and Harvard (E.A.L., O.B., T.W.Y.), Cambridge - all in Massachusetts; Charles River Laboratories, Montreal (J.D.); University of Colorado School of Medicine, Aurora (A.L.); Pendergast Consulting, Washington, DC (M.K.P.); Goldkind Consulting, Potomac, MD (S.F.G.); the Department of Neurology Feinberg School of Medicine, Northwestern University, Chicago (N.R.B., K.F., I.S., J.R.M.); the Department of Neurology, University of Rochester Medical Center, Rochester, NY (E.F.A.); Brain Hz Consulting, Del Mar, CA (C.R.); Tyndall Consulting, Wake Forest, NC (K.T.); and Brammer Bio, Alachua, FL (R.O.S.).
Mol Ther Methods Clin Dev 2019 Sep 7;14:134-147. Epub 2019 Jun 7.
Infection, Immunity and Inflammation Program, Molecular and Cellular Immunology Section, UCL Great Ormond Street Institute of Child Health, University College London, London WC1N 1EH, UK.
Exp Hematol 2019 07 28;75:53-63.e11. Epub 2019 Jun 28.
Department of Pathology, Brigham and Women's Hospital, Harvard Medical School, Boston, Massachusetts. Electronic address:
Mol Ther Methods Clin Dev 2019 Jun 6;13:399-413. Epub 2019 Apr 6.
Stem Cell & Neurotherapies Group, School of Biological Sciences, Faculty of Biology Medicine and Health, Division of Cell Matrix Biology and Regenerative Medicine, University of Manchester, Manchester M13 9PT, UK.
Blood Adv 2018 10;2(19):2505-2512
Division of Hematology/Oncology, Dana-Farber/Boston Children's Cancer and Blood Disorders Center, Boston, MA.
Genome Med 2018 09 28;10(1):70. Epub 2018 Sep 28.
Department of Microbiology, University of Pennsylvania School of Medicine, 3610 Hamilton Walk, Philadelphia, PA, 19104-6076, USA.
N Engl J Med 2017 10 4;377(17):1630-1638. Epub 2017 Oct 4.
From Massachusetts General Hospital and Harvard Medical School (F.E., P.L.M.), Dana-Farber and Boston Children's Cancer and Blood Disorders Center (C. Duncan, M.A., C. Dansereau, D.A.W.), and Boston Children's Hospital, Harvard Medical School, and Harvard Stem-Cell Institute (D.A.W.), Boston, and Bluebird Bio, Cambridge (A.M.P., E.S., T.O., D.D.) - all in Massachusetts; University of Minnesota Children's Hospital, Minneapolis (P.J.O., T.C.L., W.P.M., G.V.R.); University of California, Los Angeles, Los Angeles (S.D.O., R.S., A.J.S.); University College London Great Ormond Street Hospital Institute of Child Health and Great Ormond Street Hospital NHS Trust, London (A.J.T., H.B.G., P.G.); Pediatric Neurology Department, Hôpital Bicêtre-Hôpitaux Universitaires Paris Sud, Le Kremlin Bicêtre, France (C.S., P.A.); Fundacion Investigar, Buenos Aires (H.A.); and Women's and Children's Hospital, North Adelaide, SA, Australia (D.B., N.J.C.S.).
Sci Rep 2017 04 27;7:46731. Epub 2017 Apr 27.
Cell Processing Section, Department of Transfusion Medicine, Clinical Center; National Institutes of Health, Bethesda, Maryland, USA.
Cytotherapy 2015 Apr 4;17(4):339-43. Epub 2014 Dec 4.
University of Wisconsin, Madison, Wisconsin, USA.
Transfusion 2015 Mar 14;55(3):674-9. Epub 2014 Oct 14.
The EMMES Corporation, Rockville, Maryland.
N Engl J Med 2014 Oct;371(15):1407-17
From the Departments of Biotherapy (S.H.-B.-A., J. Blondeau, L.C., F.T., M.C.) and Immunology and Pediatric Hematology (S.B., G.C., D.M., B.N., C.P., F.T., A.F.) and the Centre d'Étude des Déficits Immunitaires (C.P.), Hôpital Necker-Enfants Malades, Assistance Publique-Hôpitaux de Paris (AP-HP), the Biotherapy Clinical Investigation Center, Groupe Hospitalier Universitaire Ouest, AP-HP, INSERM (S.H.-B.-A., J. Blondeau, L.C., F.T., M.C.), Unité de Technologies Chimiques et Biologiques pour la Santé, Centre National de la Recherche Scientifique, 8258-INSERM Unité 1022, Faculté des Sciences Pharmaceutiques et Biologiques, Université Paris Descartes (S.H.-B.-A.), Immunology Laboratory, Groupe Hospitalier Universitaire Paris-Sud, AP-HP, Le Kremlin-Bicêtre (S.H.-B.-A.), Imagine Institute, Paris Descartes-Sorbonne Paris Cité University (S.B., J. Blondeau, L.C., D.M., B.N., C.P., E.S., A.F., M.C.), INSERM Unités Mixtes de Recherche 1163, Laboratory of Human Lymphohematopoiesis (J. Blondeau, L.C., E.S., F.T., A.F., M.C.), Groupe Immunoscope, Immunology Department, Institut Pasteur (A.L.), and Collège de France (A.F.) - all in Paris; Division of Hematology-Oncology (S.-Y.P., H.B., D.G., C.E.H., G.H., L.E.L., W.B.L., D.A.W.) and Division of Immunology (L.D.N.), Boston Children's Hospital, Department of Pediatric Oncology, Dana-Farber Cancer Institute (S.-Y.P., D.G., L.E.L., W.B.L., D.A.W.), Harvard Medical School (S.-Y.P., M.A., L.E.L., W.B.L., J.R., L.E.S., A.T., L.D.N., D.A.W.), Center for Human Cell Therapy, Program in Cellular and Molecular Medicine, Boston Children's Hospital (M.A., J.R., L.E.S., A.T.), Division of Hematologic Malignancies, Dana-Farber Cancer Institute (J.R.), and the Manton Center for Orphan Disease Research (L.D.N.) - all in Boston; Great Ormond Street Hospital for Children NHS Foundation Trust (H.B.G., J.X.-B., A.J.T.) and Section of Molecular and Cellular Immunology, University College London Institute of Child Health (H.B.G., K.F.B., A.
Clin Transl Sci 2014 Apr 21;7(2):93-9. Epub 2014 Mar 21.
The EMMES Corporation, Rockville, Maryland, USA.
J Histochem Cytochem 2014 Apr 6;62(4):265-75. Epub 2014 Jan 6.
Program in Cellular and Molecular Medicine, Children's Hospital Boston and Department of Pediatrics, Harvard Medical School, Boston, Massachusetts (NSB).
Front Immunol 2013 17;4:461. Epub 2013 Dec 17.
Laboratory on Allergy, CRCHUM Notre-Dame Hospital , Montreal, QC , Canada.
Stem Cells Transl Med 2013 Nov 7;2(11):871-83. Epub 2013 Oct 7.
International Society for Cellular Therapy.
Blood 2013 Oct 30;122(17):3074-81. Epub 2013 Aug 30.
Dana-Farber Cancer Institute, Boston, MA;
Stem Cell Rev Rep 2012 Sep;8(3):696-705
Schepens Eye Research Institute, 20 Staniford Street, Boston, MA 02114, USA.
Cell Stem Cell 2011 Apr;8(4):445-58
Genetics and Gastroenterology Divisions, Brigham and Women's Hospital, Gastrointestinal Cancer Center, Dana-Farber Cancer Institute, Boston, MA 02115, USA.
Blood 2011 Apr 7;117(16):4315-22. Epub 2011 Feb 7.
Department of Medical Oncology, Dana-Farber Cancer Institute, Boston, MA 02215, USA.
J Pediatr Surg 2011 Jan;46(1):57-61
Department of Surgery, Children's Hospital Boston and Harvard Medical School, Boston, MA 02115, USA.
Front Immunol 2011 12;2:35. Epub 2011 Sep 12.
Department of Cancer Immunology and AIDS, Dana-Farber Cancer Institute Boston, MA, USA.
Mol Ther 2010 Nov 20;18(11):2028-37. Epub 2010 Jul 20.
Immune Disease Institute, Harvard Medical School, Boston, Massachusetts, USA.
J Pediatr Surg 2008 Jun;43(6):1164-9
Department of Surgery, Children's Hospital Boston, Harvard Medical School, Boston, MA 02115, USA.
J Pediatr Surg 2007 Jun;42(6):974-9; discussion 979-80
Genome Biol 2002 Jul 29;3(8):REVIEWS3011. Epub 2002 Jul 29.
Pulmonary Center, Boston University School of Medicine, Boston, MA 02118-2394, USA.