Publications by authors named "Mario Amendola"

27 Publications

  • Page 1 of 1

GATA Factor-Mediated Gene Regulation in Human Erythropoiesis.

iScience 2020 Apr 30;23(4):101018. Epub 2020 Mar 30.

Laboratory of Chromatin and Gene Regulation during Development, Imagine Institute, INSERM UMR, 1163 Paris, France; Paris Descartes, Sorbonne Paris Cité University, Imagine Institute, Paris, France. Electronic address:

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April 2020

Optimization of CRISPR/Cas9 Delivery to Human Hematopoietic Stem and Progenitor Cells for Therapeutic Genomic Rearrangements.

Mol Ther 2019 01 17;27(1):137-150. Epub 2018 Oct 17.

Genethon, INSERM UMR951, Evry 91000, France; Laboratory of Chromatin and Gene Regulation During Development, Imagine Institute, INSERM UMR1163, Paris 75015, France; Paris Descartes, Sorbonne Paris Cité University, Imagine Institute, Paris 75015, France. Electronic address:

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January 2019

Nuclear lamins are not required for lamina-associated domain organization in mouse embryonic stem cells.

EMBO Rep 2015 May 17;16(5):610-7. Epub 2015 Mar 17.

Division of Gene Regulation, Netherlands Cancer Institute, Amsterdam, the Netherlands

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May 2015

Easy quantitative assessment of genome editing by sequence trace decomposition.

Nucleic Acids Res 2014 Dec 9;42(22):e168. Epub 2014 Oct 9.

Division of Gene Regulation, Netherlands Cancer Institute, Plesmanlaan 121, 1016 HM Amsterdam, the Netherlands

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December 2014

Mechanisms and dynamics of nuclear lamina-genome interactions.

Curr Opin Cell Biol 2014 Jun 30;28:61-8. Epub 2014 Mar 30.

Division of Gene Regulation, Netherlands Cancer Institute, Amsterdam, The Netherlands. Electronic address:

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June 2014

Single-cell dynamics of genome-nuclear lamina interactions.

Cell 2013 Mar 21;153(1):178-92. Epub 2013 Mar 21.

Division of Gene Regulation, Netherlands Cancer Institute, Amsterdam, 1066 CX, The Netherlands.

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March 2013

A double-switch vector system positively regulates transgene expression by endogenous microRNA expression (miR-ON vector).

Mol Ther 2013 May 26;21(5):934-46. Epub 2013 Feb 26.

Division of Regenerative Medicine, Gene Therapy and Stem Cells, San Raffaele Scientific Institute, Milan, Italy.

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May 2013

Effects of phosphorylation and neuronal activity on the control of synapse formation by synapsin I.

J Cell Sci 2011 Nov 1;124(Pt 21):3643-53. Epub 2011 Nov 1.

San Raffaele Scientific Institute and Vita-Salute University, Via Olgettina 58, 20132 Milano, Italy.

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November 2011

Oxidative stress and cell death in cells expressing L-ferritin variants causing neuroferritinopathy.

Neurobiol Dis 2010 Jan 23;37(1):77-85. Epub 2009 Sep 23.

Division of Neuroscience, San Raffaele Scientific Institute, Via Olgettina 58, 20132 Milano, Italy.

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January 2010

Regulated and multiple miRNA and siRNA delivery into primary cells by a lentiviral platform.

Mol Ther 2009 Jun 17;17(6):1039-52. Epub 2009 Mar 17.

San Raffaele Telethon Institute for Gene Therapy, Milan, Italy.

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June 2009

Stable knockdown of microRNA in vivo by lentiviral vectors.

Nat Methods 2009 Jan 30;6(1):63-6. Epub 2008 Nov 30.

San Raffaele Telethon Institute for Gene Therapy, Via Olgettina 58, Milan, Italy.

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January 2009

Endogenous microRNA can be broadly exploited to regulate transgene expression according to tissue, lineage and differentiation state.

Nat Biotechnol 2007 Dec 16;25(12):1457-67. Epub 2007 Nov 16.

San Raffaele Telethon Institute for Gene Therapy, San Raffaele Scientific Institute, via Olgettina, 58, 20132 Milan, Italy.

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December 2007

Efficient Tet-dependent expression of human factor IX in vivo by a new self-regulating lentiviral vector.

Mol Ther 2005 May;11(5):763-75

Institute for Cancer Research and Treatment, University of Torino Medical School, Strada Provinciale 142, 10060 Candiolo, Turin, Italy.

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May 2005

Coordinate dual-gene transgenesis by lentiviral vectors carrying synthetic bidirectional promoters.

Nat Biotechnol 2005 Jan 26;23(1):108-16. Epub 2004 Dec 26.

San Raffaele Telethon Institute for Gene Therapy (HSR-TIGET), San Raffaele Scientific Institute, via Olgettina 58, 20132 Milano, Italy.

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January 2005