Publications by authors named "Maddalena Migliavacca"

19Publications

Lentiviral gene therapy corrects platelet phenotype and function in patients with Wiskott-Aldrich syndrome.

J Allergy Clin Immunol 2019 09 27;144(3):825-838. Epub 2019 Mar 27.

San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), Division of Regenerative Medicine, Stem Cells and Gene Therapy, IRCCS San Raffaele Scientific Institute, Milan, Italy; Milan Unit, Istituto di Ricerca Genetica e Biomedica, Consiglio Nazionale delle Ricerche, Milan, Italy. Electronic address:

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http://dx.doi.org/10.1016/j.jaci.2019.03.012DOI Listing
http://www.ncbi.nlm.nih.gov/pmc/articles/PMC6721834PMC
September 2019

NADPH Oxidase Deficiency: A Multisystem Approach.

Oxid Med Cell Longev 2017 21;2017:4590127. Epub 2017 Dec 21.

Department of Translational Medical Sciences, University of Naples Federico II, Naples, Italy.

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http://dx.doi.org/10.1155/2017/4590127DOI Listing
http://www.ncbi.nlm.nih.gov/pmc/articles/PMC5753020PMC
August 2018

Multiparametric Whole Blood Dissection: A one-shot comprehensive picture of the human hematopoietic system.

Cytometry A 2017 10 13;91(10):952-965. Epub 2017 Jun 13.

San Raffaele Telethon Institute for Gene Therapy (SR-TIGET), San Raffaele Scientific Institute, Milan, 20132, Italy.

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http://dx.doi.org/10.1002/cyto.a.23148DOI Listing
http://www.ncbi.nlm.nih.gov/pmc/articles/PMC5697613PMC
October 2017

Pioglitazone as a novel therapeutic approach in chronic granulomatous disease.

J Allergy Clin Immunol 2016 06 4;137(6):1913-1915.e2. Epub 2016 Apr 4.

San Raffaele Telethon Institute for Gene Therapy (TIGET), Pediatric Immunohematology and Bone Marrow Transplantation Unit, San Raffaele Scientific Institute, Milan, Italy.

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http://dx.doi.org/10.1016/j.jaci.2016.01.033DOI Listing
http://www.ncbi.nlm.nih.gov/pmc/articles/PMC4889778PMC
June 2016

Dual-regulated lentiviral vector for gene therapy of X-linked chronic granulomatosis.

Mol Ther 2014 Aug 29;22(8):1472-1483. Epub 2014 May 29.

Department of Pediatrics, Children's Hospital Bambino Gesù and University of Rome Tor Vergata School of Medicine, Rome, Italy; San Raffaele Telethon Institute for Gene Therapy (TIGET), Scientific Institute HS Raffaele, Milan, Italy. Electronic address:

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http://dx.doi.org/10.1038/mt.2014.87DOI Listing
http://www.ncbi.nlm.nih.gov/pmc/articles/PMC4435596PMC
August 2014