Publications by authors named "Lucia Sergi Sergi"

22Publications

Efficacy of lentivirus-mediated gene therapy in an Omenn syndrome recombination-activating gene 2 mouse model is not hindered by inflammation and immune dysregulation.

J Allergy Clin Immunol 2018 09 11;142(3):928-941.e8. Epub 2017 Dec 11.

San Raffaele Telethon Institute for Gene Therapy (TIGET), Division of Regenerative Medicine, Stem Cells and Gene Therapy, San Raffaele Scientific Institute, Milan, Italy; Milan Unit, Istituto di Ricerca Genetica e Biomedica, Consiglio Nazionale delle Ricerche, Milan, Italy. Electronic address:

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http://dx.doi.org/10.1016/j.jaci.2017.11.015DOI Listing
http://www.ncbi.nlm.nih.gov/pmc/articles/PMC6081264PMC
September 2018

miR-135a Inhibits Cancer Stem Cell-Driven Medulloblastoma Development by Directly Repressing Arhgef6 Expression.

Stem Cells 2015 May;33(5):1377-89

Neural Stem Cell Biology Unit, Division of Regenerative Medicine, Stem Cells and Gene Therapy, Telethon Institute for Gene Therapy, San Raffaele Scientific Institute, Milan, Italy; Vita-Salute San Raffaele University, Milan, Italy.

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http://dx.doi.org/10.1002/stem.1958DOI Listing
May 2015

Dual-regulated lentiviral vector for gene therapy of X-linked chronic granulomatosis.

Mol Ther 2014 Aug 29;22(8):1472-1483. Epub 2014 May 29.

Department of Pediatrics, Children's Hospital Bambino Gesù and University of Rome Tor Vergata School of Medicine, Rome, Italy; San Raffaele Telethon Institute for Gene Therapy (TIGET), Scientific Institute HS Raffaele, Milan, Italy. Electronic address:

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http://dx.doi.org/10.1038/mt.2014.87DOI Listing
http://www.ncbi.nlm.nih.gov/pmc/articles/PMC4435596PMC
August 2014

Epidermal growth factor receptor expression identifies functionally and molecularly distinct tumor-initiating cells in human glioblastoma multiforme and is required for gliomagenesis.

Cancer Res 2010 Oct 21;70(19):7500-13. Epub 2010 Sep 21.

Neural Stem Cell Biology Unit, Division of Regenerative Medicine, Stem Cells and Gene Therapy, San Raffaele Scientific Institute, Milan, Italy.

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http://dx.doi.org/10.1158/0008-5472.CAN-10-2353DOI Listing
October 2010

HIV-1-derived lentiviral vectors directly activate plasmacytoid dendritic cells, which in turn induce the maturation of myeloid dendritic cells.

Hum Gene Ther 2011 Feb 14;22(2):177-88. Epub 2011 Jan 14.

San Raffaele Telethon Institute for Gene Therapy (HSR-TIGET) , Department of Regenerative Medicine, Stem Cells and Gene Therapy, Via Olgettina 58, Milan, Italy.

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http://www.liebertpub.com/doi/10.1089/hum.2010.085
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http://dx.doi.org/10.1089/hum.2010.085DOI Listing
February 2011

The galactocerebrosidase enzyme contributes to the maintenance of a functional hematopoietic stem cell niche.

Blood 2010 Sep 28;116(11):1857-66. Epub 2010 May 28.

San Raffaele Telethon Institute for Gene Therapy, San Raffaele Scientific Institute, Via Olgettina 58, Milan, Italy.

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http://dx.doi.org/10.1182/blood-2009-12-256461DOI Listing
http://www.ncbi.nlm.nih.gov/pmc/articles/PMC3173985PMC
September 2010

A microRNA-regulated lentiviral vector mediates stable correction of hemophilia B mice.

Blood 2007 Dec 28;110(13):4144-52. Epub 2007 Aug 28.

San Raffaele Telethon Institute for Gene Therapy, San Raffaele Scientific Institute, Milan, Italy.

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http://dx.doi.org/10.1182/blood-2007-03-078493DOI Listing
December 2007

Endogenous microRNA regulation suppresses transgene expression in hematopoietic lineages and enables stable gene transfer.

Nat Med 2006 May 23;12(5):585-91. Epub 2006 Apr 23.

San Raffaele Telethon Institute for Gene Therapy (HSR-TIGET), via Olgettina 58, 20132 Milano, Italy.

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http://dx.doi.org/10.1038/nm1398DOI Listing
May 2006