Publications by authors named "Harald Petry"

44Publications

Targeting RNA-Mediated Toxicity in C9orf72 ALS and/or FTD by RNAi-Based Gene Therapy.

Mol Ther Nucleic Acids 2019 Jun 11;16:26-37. Epub 2019 Feb 11.

Department of Research & Development, uniQure Biopharma B.V., Amsterdam, the Netherlands. Electronic address:

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June 2019

Optimization of viral protein ratios for production of rAAV serotype 5 in the baculovirus system.

Gene Ther 2018 09 1;25(6):415-424. Epub 2018 Aug 1.

Vector Development department, research at uniQure, Paasheuvelweg 25A, 1105 BP, Amsterdam, The Netherlands.

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September 2018

Perspective on the Road toward Gene Therapy for Parkinson's Disease.

Front Neuroanat 2016 9;10:128. Epub 2017 Jan 9.

Neurobiology Research, uniQure BV Amsterdam, Netherlands.

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January 2017

Phase I open label liver-directed gene therapy clinical trial for acute intermittent porphyria.

J Hepatol 2016 10 17;65(4):776-783. Epub 2016 May 17.

Instituto de Investigación Sanitaria de Navarra (IdiSNA), Calle Irunlarrea 3, Pamplona 31008, Spain; Gene therapy and regulation of Gene Expression Program, Centro de Investigación Médica Aplicada, Universidad de Navarra, Avda. Pio XII 55, Pamplona 31008, Spain. Electronic address:

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October 2016

Recombinant AAV Integration Is Not Associated With Hepatic Genotoxicity in Nonhuman Primates and Patients.

Mol Ther 2016 06 7;24(6):1100-1105. Epub 2016 Mar 7.

Department of Translational Oncology, National Center for Tumor Diseases and German Cancer Research Center, Heidelberg, Germany. Electronic address:

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June 2016

Long-term increased carnitine palmitoyltransferase 1A expression in ventromedial hypotalamus causes hyperphagia and alters the hypothalamic lipidomic profile.

PLoS One 2014 12;9(5):e97195. Epub 2014 May 12.

Department of Biochemistry and Molecular Biology, Facultat de Farmàcia, Universitat de Barcelona and Institut de Biomedicina de la Universitat de Barcelona (IBUB) and CIBER Fisiopatología de la Obesidad y la Nutrición (CIBERobn), Instituto de Salud Carlos III, Barcelona, Spain.

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June 2015

Immune Responses to AAV-Vectors, the Glybera Example from Bench to Bedside.

Front Immunol 2014 3;5:82. Epub 2014 Mar 3.

Research and Development, uniQure B.V. , Amsterdam , Netherlands.

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March 2014

Safety profile of recombinant adeno-associated viral vectors: focus on alipogene tiparvovec (Glybera®).

Expert Rev Clin Pharmacol 2014 Jan 25;7(1):53-65. Epub 2013 Nov 25.

uniQure, Meibergdreef 61, 1105 BA Amsterdam, The Netherlands.

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January 2014